Development stage
Phase 1/2
Assets whose furthest-along trial is at this stage.
177Lu-BetaBart
RadiopharmaceuticalPhase 1/2
177Lu-DPI-4452
RadiopharmaceuticalPhase 1/2
2-hydroxybenzylamine acetate
Small moleculePhase 1/2
A2B395
Cell therapyPhase 1/2
A2B530
Cell therapyPhase 1/2
A2B543
Cell therapyPhase 1/2
A2B694
Cell therapyPhase 1/2
AAV1.SERCA2a
Gene therapy / editingPhase 1/2
AB-101
Unknown / undisclosedPhase 1/2
AB8939
Unknown / undisclosedPhase 1/2
ABBV-1758
Monoclonal antibodyPhase 1/2
ABBV-2001
Multispecific antibodyPhase 1/2
ABBV-6628
Antibody fragmentPhase 1/2
ABD-3001
Unknown / undisclosedPhase 1/2
ABT-101
Small moleculePhase 1/2
ACC017
Small moleculePhase 1/2
ACI-24.060
VaccinePhase 1/2
ACI-35.030
VaccinePhase 1/2No recent activity
AFNT-211
Small moleculePhase 1/2
AGuIX
OtherPhase 1/2
AK129
Multispecific antibodyPhase 1/2
AK138D1
Antibody–drug conjugatePhase 1/2
AL001
Small moleculePhase 1/2
ALE.P02
Antibody–drug conjugatePhase 1/2
ALE.P03
Antibody–drug conjugatePhase 1/2
ALG.APV-527
Multispecific antibodyPhase 1/2
ALN-SOD
RNA / oligonucleotidePhase 1/2
AMT-130
Small moleculePhase 1/2
AMT-260
Gene therapy / editingPhase 1/2
ANS02
Small moleculePhase 1/2
AP203
Small moleculePhase 1/2
APG-115
Unknown / undisclosedPhase 1/2
ARD103
Cell therapyPhase 1/2
ARO-ALK7
RNA / oligonucleotidePhase 1/2
ARO-C3
RNA / oligonucleotidePhase 1/2
ARO-DIMER-PA
RNA / oligonucleotidePhase 1/2
ARO-HSD
Unknown / undisclosedPhase 1/2No recent activity
ARO-INHBE
RNA / oligonucleotidePhase 1/2
ARO-MAPT-SC
RNA / oligonucleotidePhase 1/2
ARV-766
OtherPhase 1/2
ARV-806
Small moleculePhase 1/2
ASP546C
Antibody–drug conjugatePhase 1/2
ATV-1601
Small moleculePhase 1/2
AU-007
Monoclonal antibodyPhase 1/2
AVZO-021
Small moleculePhase 1/2
AVZO-023
Small moleculePhase 1/2
AVZO-1418
Antibody–drug conjugatePhase 1/2
AZD0305
Antibody–drug conjugatePhase 1/2
AZD3632
Unknown / undisclosedPhase 1/2
AZD4045
Cell therapyPhase 1/2
AZD5492
Unknown / undisclosedPhase 1/2
AZD6750
Biologic (subtype unspecified)Phase 1/2
AZD7789
Multispecific antibodyPhase 1/2
AZD8205
Antibody–drug conjugatePhase 1/2
Adipose-derived MSC clusters (S.Biomedics)
Cell therapyPhase 1/2
Alintegimod
Small moleculePhase 1/2
Anti-CD33 CAR T-cells
Biologic (subtype unspecified)Phase 1/2
BA3071
Biologic (subtype unspecified)Phase 1/2
BAY 3713372
Small moleculePhase 1/2
BBT-207
Small moleculePhase 1/2
BBT001
Multispecific antibodyPhase 1/2
BBT002
Multispecific antibodyPhase 1/2
BCMA CAR-NK (Hrain)
Cell therapyPhase 1/2
BCMA CAR-NK (Shenzhen Pregene Biopharma)
Cell therapyPhase 1/2
BCMA-CART (Bioray Laboratories)
Cell therapyPhase 1/2
BCMA-targeted Prime CAR-T cells (Chongqing Precision Biotech)
Cell therapyPhase 1/2
BDTX-1535
Small moleculePhase 1/2
BEAM-301
Gene therapy / editingPhase 1/2
BEAM-302
Gene therapy / editingPhase 1/2
BEBT-701
RNA / oligonucleotidePhase 1/2
BG1805
Biologic (subtype unspecified)Phase 1/2
BGB-B2033
Multispecific antibodyPhase 1/2
BGC101
Cell therapyPhase 1/2
BH-30643
Small moleculePhase 1/2
BI-1910
Monoclonal antibodyPhase 1/2
BIIB105
Unknown / undisclosedPhase 1/2
BL-M02D1
Antibody–drug conjugatePhase 1/2
BLEX 404
Protein / enzyme therapeuticPhase 1/2
BLU-924
Small moleculePhase 1/2
BMN 351
RNA / oligonucleotidePhase 1/2
BMS-986158
Small moleculePhase 1/2
BMS-986449
Small moleculePhase 1/2
BMS-986490
Small moleculePhase 1/2
BMS-986523
Small moleculePhase 1/2
BPI-1178
Small moleculePhase 1/2
BPI-361175
Small moleculePhase 1/2
BPI-572270
Small moleculePhase 1/2
BSB-1001
Cell therapyPhase 1/2
BT02
Monoclonal antibodyPhase 1/2
BT5528
PeptidePhase 1/2
Beijing Biotech BCMA/CD19 dual-target CAR-T
Cell therapyPhase 1/2
Beijing Biotech BCMA/CD38 dual-target CAR-T
Cell therapyPhase 1/2
Beijing Biotech BCMA/GPRC5D dual-target CAR-T
Cell therapyPhase 1/2
Beijing Biotech anti-CD19 CAR-T
Cell therapyPhase 1/2
Bexmarilimab
Monoclonal antibodyPhase 1/2
BioTTT001
OtherPhase 1/2
CAB-ROR2-ADC
Monoclonal antibodyPhase 1/2
CAN04
Monoclonal antibodyPhase 1/2
CART84
Cell therapyPhase 1/2
CC-223
Small moleculePhase 1/2
CCTx-001
Cell therapyPhase 1/2
CD123 targeted CAR-NK cells
Cell therapyPhase 1/2
CD123/CD33 CART
Cell therapyPhase 1/2
CDNF (cerebral dopamine neurotrophic factor)
Biologic (subtype unspecified)Phase 1/2No recent activity
CFI-400945
Unknown / undisclosedPhase 1/2
CID-103
Monoclonal antibodyPhase 1/2
CIS-DPI
Small moleculePhase 1/2
CJRB-101
Microbiome therapeuticPhase 1/2
CKD-703
Antibody–drug conjugatePhase 1/2
CM313
Monoclonal antibodyPhase 1/2
CP-383
Small moleculePhase 1/2
CR-001
Multispecific antibodyPhase 1/2
CRG-150
Cell therapyPhase 1/2
CRMA-1001
Cell therapyPhase 1/2
CS32582
Small moleculePhase 1/2
CT071
Cell therapyPhase 1/2
CTS2190
Small moleculePhase 1/2
CTX-712
Unknown / undisclosedPhase 1/2
CTX112
Biologic (subtype unspecified)Phase 1/2
CTX131
Cell therapyPhase 1/2
CWP232291
Unknown / undisclosedPhase 1/2
CYNK-001
Cell therapyPhase 1/2No recent activity
Cariprazine long-acting injection (Mapi Pharma)
Small moleculePhase 1/2
Ciforadenant
Small moleculePhase 1/2
DB-1310
Antibody–drug conjugatePhase 1/2
DISC-0974
Monoclonal antibodyPhase 1/2
DNL126
Protein / enzyme therapeuticPhase 1/2
DS-1103a
Unknown / undisclosedPhase 1/2
DS-3939a
Unknown / undisclosedPhase 1/2
DS-7011a
Unknown / undisclosedPhase 1/2
DSP-1083
Cell therapyPhase 1/2
DSP107
Monoclonal antibodyPhase 1/2
DZD6008
Small moleculePhase 1/2
Debio 0123
Small moleculePhase 1/2
Debio 1562M
Unknown / undisclosedPhase 1/2
Decoy20
Microbiome therapeuticPhase 1/2
Dositinib mesylate
Small moleculePhase 1/2
Dual-target Car-nk Cells
Cell therapyPhase 1/2
EB-SELECT Dual-Target CAR-NK Cells
Cell therapyPhase 1/2
EB-SELECT Single-Target CAR-NK Cells
Cell therapyPhase 1/2
EC5026
Small moleculePhase 1/2
ECI830
Small moleculePhase 1/2
EDIT-301
Cell therapyPhase 1/2
ELE-101
Small moleculePhase 1/2
ENV-501
Antibody–drug conjugatePhase 1/2
EP0031
Small moleculePhase 1/2
EP0042
Unknown / undisclosedPhase 1/2
EP0062
Small moleculePhase 1/2
ETX101
Gene therapy / editingPhase 1/2
EVM14
VaccinePhase 1/2
EcoActive
Microbiome therapeuticPhase 1/2
Elironrasib
Small moleculePhase 1/2
Eltanexor
Unknown / undisclosedPhase 1/2
Enzomenib
Small moleculePhase 1/2
FMC-376
Small moleculePhase 1/2
FWD1802
Small moleculePhase 1/2
Forimtamig
Multispecific antibodyPhase 1/2
GEN-725
Small moleculePhase 1/2
GEN1042
Biologic (subtype unspecified)Phase 1/2
GFH276
Small moleculePhase 1/2
GH21
Small moleculePhase 1/2
GI-101
Protein / enzyme therapeuticPhase 1/2
GI-101A
Multispecific antibodyPhase 1/2
GI-108
Multispecific antibodyPhase 1/2
GIC-102
Cell therapyPhase 1/2
GK1-399 (formerly TTP399)
Small moleculePhase 1/2No recent activity
GLPG5101
Cell therapyPhase 1/2
GNC-035
Multispecific antibodyPhase 1/2
GNS561
Small moleculePhase 1/2
GRWD5769
Small moleculePhase 1/2
GSK2857914
Monoclonal antibodyPhase 1/2
GSK5926371
Biologic (subtype unspecified)Phase 1/2
GUB-UCN2
PeptidePhase 1/2
GVV858
Unknown / undisclosedPhase 1/2
H002
Small moleculePhase 1/2
H3B-6545
Small moleculePhase 1/2
HB0036
Multispecific antibodyPhase 1/2
HEC169096
Small moleculePhase 1/2
HL-300
Small moleculePhase 1/2
HLX208 + HLX10
CombinationPhase 1/2
HLX301
Multispecific antibodyPhase 1/2
HMBD-001
Monoclonal antibodyPhase 1/2
HS-001
Cell therapyPhase 1/2
HS235
PeptidePhase 1/2
HYP-6589
Small moleculePhase 1/2
Hebei Senlang CD7 CAR-T
Cell therapyPhase 1/2
Hepadvax
VaccinePhase 1/2
HuL001
Monoclonal antibodyPhase 1/2
HucMSC intramyocardial therapy
Cell therapyPhase 1/2
Human Serum Albumin/interferon alpha2b fusion protein
Biologic (subtype unspecified)Phase 1/2No recent activity
IAP0971
Small moleculePhase 1/2
ICP-490
Small moleculePhase 1/2
IDE397
Small moleculePhase 1/2
IDP-001
Antibody–drug conjugatePhase 1/2
IDP-023
Cell therapyPhase 1/2
IDP-121
Small moleculePhase 1/2
IMM-1-104
Small moleculePhase 1/2
IMT-009
Monoclonal antibodyPhase 1/2
INO-3107
Gene therapy / editingPhase 1/2No recent activity
INV-6452
Small moleculePhase 1/2
INV-8989
Small moleculePhase 1/2
IOA-244
Small moleculePhase 1/2
ION337
RNA / oligonucleotidePhase 1/2
IOV-4001
Cell therapyPhase 1/2
IRL757
Small moleculePhase 1/2
ITU512
Unknown / undisclosedPhase 1/2
ImmuneOnco anti-PAH candidate (IMC-003)
Biologic (subtype unspecified)Phase 1/2
JAB-23E73
Small moleculePhase 1/2
JAB-8263
Small moleculePhase 1/2
JIN-A02
Small moleculePhase 1/2
JK08
Protein / enzyme therapeuticPhase 1/2
JL18008
Protein / enzyme therapeuticPhase 1/2
JMT202
Unknown / undisclosedPhase 1/2
JS111 AP-L1898
Small moleculePhase 1/2
JX11502MA
Small moleculePhase 1/2No recent activity
KB707
Gene therapy / editingPhase 1/2
KIT2014
PeptidePhase 1/2
KL590586
Small moleculePhase 1/2
KQ-2003
Cell therapyPhase 1/2
L-DOS47
Antibody–drug conjugatePhase 1/2
LBL-034
Unknown / undisclosedPhase 1/2
LCB84
Antibody–drug conjugatePhase 1/2
LM11A-31
Small moleculePhase 1/2
LP-184
Small moleculePhase 1/2
LP-98
PeptidePhase 1/2
LT-002-158
Protein / enzyme therapeuticPhase 1/2
LW231
Unknown / undisclosedPhase 1/2
LX1001
Gene therapy / editingPhase 1/2
LYL273
Small moleculePhase 1/2
LYT-200
Monoclonal antibodyPhase 1/2
MB-001
Monoclonal antibodyPhase 1/2
MBS314
Unknown / undisclosedPhase 1/2
MDNA11
Protein / enzyme therapeuticPhase 1/2
MET-233i
PeptidePhase 1/2
MRT-2359
Small moleculePhase 1/2
MRX-2843
Small moleculePhase 1/2
Melevodopa/carbidopa (Sirio)
Small moleculePhase 1/2No recent activity
Menstrual blood-derived mesenchymal stem cells (MenSCs)
Cell therapyPhase 1/2No recent activity
N17350
Biologic (subtype unspecified)Phase 1/2
NDI-101150
Small moleculePhase 1/2
NEO212
Small moleculePhase 1/2
NGM707
Unknown / undisclosedPhase 1/2
NSC001
Small moleculePhase 1/2
Nula-cel
Cell therapyPhase 1/2
OBX-115
Biologic (subtype unspecified)Phase 1/2
ODX (Osteodex)
Unknown / undisclosedPhase 1/2
OPC-415
Cell therapyPhase 1/2
OPK-88006
Unknown / undisclosedPhase 1/2
OR502
Monoclonal antibodyPhase 1/2
ORIC-114
Small moleculePhase 1/2
OSE-279
VaccinePhase 1/2
OrcaGraft (Orca-Q)
Unknown / undisclosedPhase 1/2
OriCAR-017
Cell therapyPhase 1/2
PA1010
Unknown / undisclosedPhase 1/2No recent activity
PB-718
PeptidePhase 1/2
PDC*lung01
VaccinePhase 1/2
PH009-1
Small moleculePhase 1/2
PR001 (LY3884961)
Gene therapy / editingPhase 1/2
PRAX-222
RNA / oligonucleotidePhase 1/2
PT-112
Small moleculePhase 1/2
PT199
Monoclonal antibodyPhase 1/2
PYX-201
Small moleculePhase 1/2
Pamlectabart tismanitin
OtherPhase 1/2
Pegenzileukin
Protein / enzyme therapeuticPhase 1/2
Pepinemab
Monoclonal antibodyPhase 1/2
PolyCore
OtherPhase 1/2
QLC1101
Small moleculePhase 1/2
QLS1304
Small moleculePhase 1/2
QLS5132
Unknown / undisclosedPhase 1/2
Quaratusugene Ozeplasmid
Gene therapy / editingPhase 1/2
R289
Small moleculePhase 1/2
REGN17372
Multispecific antibodyPhase 1/2
REGN5093
Monoclonal antibodyPhase 1/2
REGN5459
Multispecific antibodyPhase 1/2
REGN7945
Multispecific antibodyPhase 1/2
REM-422
Unknown / undisclosedPhase 1/2
RGT-419B
Small moleculePhase 1/2
RM-718
PeptidePhase 1/2
RMC-9805
Small moleculePhase 1/2
RN0361
RNA / oligonucleotidePhase 1/2
RNDP-001
Cell therapyPhase 1/2
S230815
RNA / oligonucleotidePhase 1/2
S241656
Small moleculePhase 1/2
S243249
Unknown / undisclosedPhase 1/2
SAR402663
Gene therapy / editingPhase 1/2
SAR439459
Biologic (subtype unspecified)Phase 1/2
SAR443579
Biologic (subtype unspecified)Phase 1/2
SAR446597
Gene therapy / editingPhase 1/2
SCM-AGH
Cell therapyPhase 1/2No recent activity
SENL103
Cell therapyPhase 1/2
SG2918
Biologic (subtype unspecified)Phase 1/2
SL-28
Biologic (subtype unspecified)Phase 1/2
SLS009
Small moleculePhase 1/2
SNK01
Cell therapyPhase 1/2
SNS-101
Monoclonal antibodyPhase 1/2
SRP-1001
RNA / oligonucleotidePhase 1/2
SRP-1003
RNA / oligonucleotidePhase 1/2
SRSD216
RNA / oligonucleotidePhase 1/2
ST-067
Biologic (subtype unspecified)Phase 1/2
STAR0602
Multispecific antibodyPhase 1/2
STI-6129
Antibody–drug conjugatePhase 1/2
STK-001
RNA / oligonucleotidePhase 1/2
STK-012
Protein / enzyme therapeuticPhase 1/2
STMC-103H
Microbiome therapeuticPhase 1/2
STX-241
Small moleculePhase 1/2
STX-721
Small moleculePhase 1/2
SYS6090
Protein / enzyme therapeuticPhase 1/2
Sea-tgt
Monoclonal antibodyPhase 1/2
Surzetoclax
Small moleculePhase 1/2
T3011
Monoclonal antibodyPhase 1/2
TAS0953
Small moleculePhase 1/2
TB511
PeptidePhase 1/2
TE-8105
PeptidePhase 1/2
TED-A9 (A9-DPC)
Cell therapyPhase 1/2
TGRX-814
Unknown / undisclosedPhase 1/2
TH9619
Small moleculePhase 1/2
TILT-123
OtherPhase 1/2
TNG260
Small moleculePhase 1/2
TNG456
Small moleculePhase 1/2
TNG462
Small moleculePhase 1/2
TNG908
Small moleculePhase 1/2
TQA3038
Unknown / undisclosedPhase 1/2
TSN1611
Small moleculePhase 1/2
TT-10
Small moleculePhase 1/2
TT-4
Small moleculePhase 1/2
TUB-030
Antibody–drug conjugatePhase 1/2
Temferon
Gene therapy / editingPhase 1/2
Trovocabtagene autoleucel (C-CAR088)
Cell therapyPhase 1/2
Tuspetinib
Small moleculePhase 1/2
U32 CAR-T
Cell therapyPhase 1/2
UX-DA003
Cell therapyPhase 1/2
VENT-02
Small moleculePhase 1/2
VERT-002
Monoclonal antibodyPhase 1/2
VGN-R08b
Gene therapy / editingPhase 1/2
VIC-1911
Small moleculePhase 1/2
VLS-1488
Small moleculePhase 1/2
VMD-102
Small moleculePhase 1/2
VMD-928
Small moleculePhase 1/2
VRN110755
Small moleculePhase 1/2
VSV-IFNβ-NIS
OtherPhase 1/2
VT3989
Small moleculePhase 1/2
VX-264
Cell therapyPhase 1/2
VX-522
RNA / oligonucleotidePhase 1/2
VY7523
Monoclonal antibodyPhase 1/2
WEF-001
Monoclonal antibodyPhase 1/2
WVE-003
RNA / oligonucleotidePhase 1/2
WVE-006
RNA / oligonucleotidePhase 1/2
WVE-007
RNA / oligonucleotidePhase 1/2
WVE-N531
RNA / oligonucleotidePhase 1/2
XS-411
Cell therapyPhase 1/2
XTX501
Multispecific antibodyPhase 1/2
XYA02
Antibody–drug conjugatePhase 1/2
XZP-5955
Small moleculePhase 1/2
XmAb942
Monoclonal antibodyPhase 1/2
YH32364
Multispecific antibodyPhase 1/2
YH42946
Small moleculePhase 1/2
ZG005
Biologic (subtype unspecified)Phase 1/2
Zevorcabtagene autoleucel
Cell therapyPhase 1/2
aritinercept
Protein / enzyme therapeuticPhase 1/2
atamparib
Small moleculePhase 1/2
birtamimab
Monoclonal antibodyPhase 1/2No recent activity
budoprutug
Monoclonal antibodyPhase 1/2
fludarabine/cyclophosphamide
Small moleculePhase 1/2
lirafugratinib
Small moleculePhase 1/2
mRNA-2808
RNA / oligonucleotidePhase 1/2
rezatapopt
Small moleculePhase 1/2
roginolisib
Small moleculePhase 1/2