Asset profile

RGX-314

Gene therapy / editing

Phase 3underway

Evidence outlook · registrational

Age-Related Macular Degeneration: registrational readout pending

Entered Phase 3 on weak signal mid-stage evidence. Registrational readout expected around 2026-10.

NCT04832724: The study enrolled 60 participants into sequential RGX-314 dose and formulation groups without randomization, blinding, or a comparator arm. Its primary endpoint was the surrogate pharmacodynamic measure of RGX-314 protein concentration, and no primary outcome results are available.

How the evidence outlook works ↗

Upcoming events

(3 total)

Estimated primary-completion dates from ClinicalTrials.gov — registry estimates, never confirmed readout dates; they can move as trials progress.

2026 (2)
October 2026 (1)
Phase 3Age-Related Macular DegenerationActive not recruiting
Est. primary completion 2026-10 · NCT05407636 · CT.gov ↗
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Research analysis

Source-grounded endpoint goals, benchmarks, comparator context, and caveats for this readout are included with Research.

December 2026 (1)
Phase 2/3Age-Related Macular DegenerationActive not recruiting
Est. primary completion 2026-12 · NCT04704921 · CT.gov ↗
What to watch

Research analysis

Source-grounded endpoint goals, benchmarks, comparator context, and caveats for this readout are included with Research.

2028 (1)
December 2028 (1)
Phase 2Age-Related Macular DegenerationEnrolling by invitation
Est. primary completion 2028-12 · NCT03999801 · CT.gov ↗
What to watch

Research analysis

Source-grounded endpoint goals, benchmarks, comparator context, and caveats for this readout are included with Research.

See the full readout calendar ↗

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