Mechanism

C9ORF72 (chromosome 9 open reading frame 72)

Assets acting on this target.

Class
Antisense oligonucleotide targeting C9ORF72
Notes
mechanism wave 2026-08-24 (DeepSeek draft; registry text of NCT04288856 names the target); source: https://clinicaltrials.gov/study/NCT04288856

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