Asset profile

Vatiquinone (PTC743)

Small molecule

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Phase 3underway

Evidence outlook · registrational

Friedreich Ataxia: registrational readout pending

Its supporting mid-stage evidence has not yet been graded on this platform. Registrational readout expected around 2027-12-31.

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Competitive landscape

No competitors sharing a mechanism or indication in the current universe.

Upcoming events

(2 total)

Estimated primary-completion dates from ClinicalTrials.gov. These are registry estimates, never confirmed readout dates; they can move as trials progress.

2027 (1)
December 2027 (1)
Phase 3Friedreich AtaxiaActive not recruiting
Est. primary completion 2027-12-31 · NCT05515536 · CT.gov ↗
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2029 (1)
March 2029 (1)
Phase 3Friedreich's AtaxiaNot yet recruiting
Est. primary completion 2029-03-15 · NCT07681713 · CT.gov ↗
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See the full readout calendar ↗

All registered studies

Every ClinicalTrials.gov study of this drug's own program, grouped by indication and phase. Research unlocks the studies themselves: titles, statuses, dates and featured-trial cross-links.

Phase 3 (3)
Phase 2/3 (2)
Phase 2 (11)
Phase 1/2 (1)
Phase 1 (1)